文章基本信息
- 标题：Risks of long-term port use in enzyme replacement therapy for lysosomal storage disorders
- 本地全文：下载
- 作者：Christian J. Hendriksz ; Paul Harmatz ; Roberto Giugliani 等
- 期刊名称：Molecular Genetics and Metabolism Reports
- 印刷版ISSN：2214-4269
- 出版年度：2018
- 卷号：15
- 页码：71-73
- DOI：10.1016/j.ymgmr.2018.02.007
- 出版社：Elsevier B.V.
- 摘要：
Totally implantable vascular access devices (TIVADs) are commonly used in conjunction with enzyme replacement therapy (ERT) for lysosomal storage disorders (LSDs). This case series describes potential complications associated with long-term TIVAD use, such as compromise of skin integrity, infection, or port failures. Best practices and skilled specialists are essential for minimizing complications from long-term TIVAD use for ERT.
- 关键词：Mucopolysaccharidosis ; Enzyme replacement therapy ; Totally implantable venous access device ; Lysosomal storage disorder
