首页    期刊浏览 2024年11月26日 星期二
登录注册

文章基本信息

  • 标题:Recurrent rhabdomyolysis caused by carnitine palmitoyltransferase II deficiency, common but under-recognised: Lessons to be learnt
  • 本地全文:下载
  • 作者:M. Balasubramanian ; T.M. Jenkins ; R.J. Kirk
  • 期刊名称:Molecular Genetics and Metabolism Reports
  • 印刷版ISSN:2214-4269
  • 出版年度:2018
  • 卷号:15
  • 页码:69-70
  • DOI:10.1016/j.ymgmr.2018.02.008
  • 出版社:Elsevier B.V.
  • 摘要:

    We discuss two adult siblings who presented with symptoms of myalgia and rhabdomyolysis following exercise with myoglobinuria; genetic testing confirmed carnitine palmitoyltransferase II deficiency and resulted in institution of appropriate crisis management and dietary advice. We explore the phenotypic variability of this commonest fatty oxidation defect that remains under-diagnosed in the adult population and provide clues for early recognition and diagnosis.

  • 关键词:Myoglobinuria ; CPT II deficiency ; Autosomal recessive ; Genetic counselling ; Dietary advice ; Rhabdomyolysis ; Myopathy
国家哲学社会科学文献中心版权所有